Detalhe da pesquisa
1.
Exagamglogene Autotemcel for Transfusion-Dependent ß-Thalassemia.
N Engl J Med
; 390(18): 1663-1676, 2024 May 09.
Artigo
em Inglês
| MEDLINE | ID: mdl-38657265
2.
Exagamglogene Autotemcel for Severe Sickle Cell Disease.
N Engl J Med
; 390(18): 1649-1662, 2024 May 09.
Artigo
em Inglês
| MEDLINE | ID: mdl-38661449
3.
Outcomes of HLA-mismatched HSCT with TCRαß/CD19 depletion or post-HSCT cyclophosphamide for inborn errors of immunity.
Blood
; 2024 Apr 26.
Artigo
em Inglês
| MEDLINE | ID: mdl-38669631
4.
Autologous gene therapy for hemoglobinopathies: From bench to patient's bedside.
Mol Ther
; 32(5): 1202-1218, 2024 May 01.
Artigo
em Inglês
| MEDLINE | ID: mdl-38454604
5.
Hematopoietic stem cell transplantation for Wiskott-Aldrich syndrome: an EBMT Inborn Errors Working Party analysis.
Blood
; 139(13): 2066-2079, 2022 03 31.
Artigo
em Inglês
| MEDLINE | ID: mdl-35100336
6.
Hematopoietic stem cell transplantation for adolescents and adults with inborn errors of immunity: an EBMT IEWP study.
Blood
; 140(14): 1635-1649, 2022 10 06.
Artigo
em Inglês
| MEDLINE | ID: mdl-35344580
7.
Approaches for bridging therapy prior to chimeric antigen receptor T cells for relapsed/refractory acute lymphoblastic B-lineage leukaemia in children and young adults.
Haematologica
; 2024 Feb 15.
Artigo
em Inglês
| MEDLINE | ID: mdl-38356450
8.
Automated production of specific T cells for treatment of refractory viral infections after allogeneic stem cell transplantation.
Haematologica
; 108(8): 2080-2090, 2023 08 01.
Artigo
em Inglês
| MEDLINE | ID: mdl-36794500
9.
[Updated AWMF Guideline on the Diagnosis and Treatment of Langerhans cell Histiocytosis in Children and Adolescents]. / Aktualisierte AWMF Leitlinie zur Diagnostik und Therapie der Langerhanszell Histiozytose (LCH) im Kindes- und Jugendalter.
Klin Padiatr
; 235(6): 322-330, 2023 Nov.
Artigo
em Alemão
| MEDLINE | ID: mdl-37666270
10.
Hematopoietic cell transplantation in severe combined immunodeficiency: The SCETIDE 2006-2014 European cohort.
J Allergy Clin Immunol
; 149(5): 1744-1754.e8, 2022 05.
Artigo
em Inglês
| MEDLINE | ID: mdl-34718043
11.
CDK6 is an essential direct target of NUP98 fusion proteins in acute myeloid leukemia.
Blood
; 136(4): 387-400, 2020 07 23.
Artigo
em Inglês
| MEDLINE | ID: mdl-32344427
12.
Extended clinical and immunological phenotype and transplant outcome in CD27 and CD70 deficiency.
Blood
; 136(23): 2638-2655, 2020 12 03.
Artigo
em Inglês
| MEDLINE | ID: mdl-32603431
13.
Risk factors for mixed chimerism in children with hemophagocytic lymphohistiocytosis after reduced toxicity conditioning.
Pediatr Blood Cancer
; 67(9): e28523, 2020 09.
Artigo
em Inglês
| MEDLINE | ID: mdl-32618429
14.
Pediatric acute graft-versus-host disease prophylaxis and treatment: surveyed real-life approach reveals dissimilarities compared to published recommendations.
Transpl Int
; 33(7): 762-772, 2020 07.
Artigo
em Inglês
| MEDLINE | ID: mdl-32133691
15.
Clearance of Treatment Refractory Adenoviremia via Adenovirus-specific Donor T-Cell Transfer During Aplasia After αßTCR-CD19-Depleted Stem Cell Transplantation.
Clin Infect Dis
; 68(8): 1406-1409, 2019 04 08.
Artigo
em Inglês
| MEDLINE | ID: mdl-30357314
16.
Clearance of Hematologic Malignancies by Allogeneic Cytokine-Induced Killer Cell or Donor Lymphocyte Infusions.
Biol Blood Marrow Transplant
; 25(7): 1281-1292, 2019 07.
Artigo
em Inglês
| MEDLINE | ID: mdl-30878607
17.
CRISPR-Cas9 Gene Editing for Sickle Cell Disease and ß-Thalassemia.
N Engl J Med
; 384(23): e91, 2021 Jun 10.
Artigo
em Inglês
| MEDLINE | ID: mdl-34107195
18.
Ex vivo drug response profiling detects recurrent sensitivity patterns in drug-resistant acute lymphoblastic leukemia.
Blood
; 129(11): e26-e37, 2017 03 16.
Artigo
em Inglês
| MEDLINE | ID: mdl-28122742
19.
Allogeneic hematopoietic stem cell transplantation from unrelated donors is associated with higher infection rates in children with acute lymphoblastic leukemia-A prospective international multicenter trial on behalf of the BFM-SG and the EBMT-PDWP.
Am J Hematol
; 94(8): 880-890, 2019 08.
Artigo
em Inglês
| MEDLINE | ID: mdl-31095771
20.
Outcome of hematopoietic cell transplantation for DNA double-strand break repair disorders.
J Allergy Clin Immunol
; 141(1): 322-328.e10, 2018 01.
Artigo
em Inglês
| MEDLINE | ID: mdl-28392333